Clinical Trials for Personalized Medicine: Design and Data Analysis
Clinical Trials for Personalized Medicine: Design and Data Analysis
In this article, we provide an overview of statistical methods for design and analysis of clinical trials for personalized medicine. In a basic setting where marker-defined subgroups are well defined based on a baseline biomarker, enrichment, marker-stratified, and strategy-based clinical trial designs, as well as related data analysis methods, are …